CHOP Gene Therapy Experts Profiled in Philadelphia Magazine
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CHOP researchers were interviewed as a part of a comprehensive article about cell and gene therapy in Philadelphia Magazine.
Hemophilia and Bleeding Disorders Program News and Updates
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CHOP-led Research Study Identifies Key Target in Treatment-Resistant Hemophilia A
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CHOP researchers have identified BAFF as a key target that may be responsible for treatment failure in about 30% of patients with hemophilia A.
Researchers Uncover A Previously Underappreciated Mechanism that Turns Off Clotting Factor in Hemophilia A
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CHOP researchers identified an in vivo role for activated protein C (APC), which could potentially be exploited for future hemophilia A treatments.
CHOP Volunteers Make Camp Special
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CHOP volunteers make camp a reality for many kids with special medical needs. They not only keep them healthy, but they also take part of the activities and enjoy seeing kids being kids.
Gene-based Clotting Factor Prevents Bleeding in Animals with Hemophilia
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A laboratory study may set the stage for a new preventive treatment for hemophilia patients who now develop antibodies to the standard treatment and then require a bypass therapy.
CHOP Investigator and Experimental One-dose Gene Therapy for Hemophilia B Featured in The New York Times
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CHOP breakthrough helps scientists edge closer to defeating a longtime enemy of human health: hemophilia, the inability to form blood clots.
One-dose Gene Therapy Produces Clotting Factor, Safely Stops Bleeding in Hemophilia B Patients
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A team of gene therapy researchers has reported on a highly active gene variant that achieved sustained factor levels in 10 adults, with no adverse effects.
Washington Post Reports on Hemophilia B Gene Therapy Advance
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A clinical trial of a gene therapy for hemophilia B is allowing patients to avoid painful, disabling internal bleeds.
3 CHOP Scientists Win Bayer Grants for Hemophilia Research
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Three CHOP researchers recently won grants for their work on hemophilia from the Bayer Hemophilia Awards Program.
After One Dose of Gene Therapy Hemophilia B Patients Maintain Near-normal Levels of Clotting Factor
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In a clinical trial led by a CHOP researcher, adult patients with hemophilia B were able to pursue daily activities without disabling bleeds.